Search for Clinical Trial Results
Mucopolysaccharidosis IV - 25 Studies Found
Status | Study |
Enrolling by invitation |
Study Name: BMN 110 Phase 3B in Australian Patients Condition: Mucopolysaccharidosis IVA (Morquio A Syndrome) Date: 2013-09-10 Interventions: Drug: BMN 110 All pateints receive treatment with BMN 110 |
Terminated |
Study Name: Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation Condition:
Date: 2012-09-17 Interventions: Drug: BMN 110 Drug will be delivered through a 4 hour (approximate) IV infusion at a dosage amount of 2. |
Terminated |
Study Name: Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome Condition:
Date: 2012-05-24 Interventions: |
Completed |
Study Name: Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome) Condition:
Date: 2011-12-22 Interventions: Drug: BMN 110 Patients will receive intravenous (IV) infusions of study drug at a dose of 2.0 mg/kg/wk o |
Enrolling by invitation |
Study Name: Immunodeficiency in Cartilage-hair Hypoplasia: Sub-project on Safety of Vaccination Against Chickenpox Condition: Cartilage-hair Hypoplasia Date: 2015-02-10 Interventions: Biological: Varilrix Vaccination against varicella in selected cartilage-hair hypoplasia patients |